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Β-Thalassemias | NEJM
Β-Thalassemias | NEJM

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia

IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article

PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm

Β-Thalassemias | NEJM
Β-Thalassemias | NEJM

Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells

Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports

Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy

Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink

Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia
Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia

Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases

Frontiers | New Insights Into Pathophysiology of β-Thalassemia
Frontiers | New Insights Into Pathophysiology of β-Thalassemia

Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica

Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review

Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health

Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica

Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells

β-Thalassemia | Genetics in Medicine
β-Thalassemia | Genetics in Medicine

IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?
IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?

Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis

Introductory Chapter: β-Thalassemia | IntechOpen
Introductory Chapter: β-Thalassemia | IntechOpen

Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects

PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar
PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar